Adaptive and innovative study design in rare diseases

Athimalaipet V Ramanan*, James M S Wason

*Corresponding author for this work

Research output: Contribution to journalArticle (Academic Journal)peer-review

Original languageEnglish
Pages (from-to)1-3
Number of pages3
JournalArchives of Disease in Childhood
Volume110
Issue number1
Early online date5 Jun 2024
DOIs
Publication statusE-pub ahead of print - 5 Jun 2024

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